“This achievement is another demonstration of our continued progress in the clinical development of our three product candidates for the treatment of X-linked retinitis pigmentosa and achromatopsia ...
About Achromatopsia Achromatopsia is an inherited retinal disorder that specifically prevents cone photoreceptors from functioning. ACHM is characterized by severely reduced visual acuity of 20/200 or ...
About AAV-CNGA3 AAV-CNGA3 is a gene therapy treatment being developed as a potential treatment for patients with achromatopsia (ACHM) due to mutations in the CNGA3 gene. Delivered via subretinal ...